Research Articles | Aplastic Anemia & MDS International Foundation

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Research Articles

Article Title Original Publication Date Journal Bone Marrow Disease
Ravulizumab: a novel C5 inhibitor for the treatment of paroxysmal nocturnal hemoglobinuria Sep 2019 Therapeutic Advances in Hematology paroxysmal nocturnal hemoglobinuria (PNH)
Germline DDX41 mutations define a significant entity within adult MDS/AML patients Sep 2019 Blood myelodysplastic syndromes (MDS)
Phase 2 Study of the ALK5 Inhibitor Galunisertib in Very Low-, Low-, and Intermediate-Risk Myelodysplastic Syndromes Sep 2019 Clinical Cancer Research: an official Journal of the American Association of Cancer Research myelodysplastic syndromes (MDS)
Management of aplastic anemia after failure of frontline immunosuppression Jul 2019 Expert Review of Hematology aplastic anemia
Defining the Boundary Between Myelodysplastic Syndromes and Myeloproliferative Neoplasms Jul 2019 Surgical Pathology Clinic myelodysplastic syndromes (MDS)
A genomics-informed computational biology platform prospectively predicts treatment responses in AML and MDS patients Jun 2019 Blood Advances myelodysplastic syndromes (MDS)
Activin Receptor II Ligand Traps: New Treatment Paradigm for Low-Risk MDS Jun 2019 Current Hematologic Malignancy Report myelodysplastic syndromes (MDS)
RBC transfusion independence among lower risk MDS patients receiving hypomethylating agents: a population-level analysis Jun 2019 Leukemia & Lymphoma myelodysplastic syndromes (MDS)
Guadecitabine (SGI-110) in patients with intermediate or high-risk myelodysplastic syndromes: phase 2 results from a multicentre, open-label, randomised, phase 1/2 trial Jun 2019 The Lancet Haematology myelodysplastic syndromes (MDS)
The case for upfront HLA-matched unrelated donor HCT as a curative option for adult acquired severe aplastic anemia: Upfront MUD HCT for adult severe aplastic anemia May 2019 Biology of Blood and Marrow Transplantation: Journal of the American Society of Blood and Marrow Transplantation aplastic anemia